Owner Shire Human Genetic Therapies, Inc.

Inventors Selden, Richard F.; Borowski, Marianne; Gillespie, Frances P.; Kinoshita, Carol M.; Treco, Douglas A.; Williams, Melanie D.

Agent Griffith Hack

Pub. Number AU-A-2012227349

Parent 2008200265

Filing date 26 September 2012

Wipo publication date 18 October 2012

C12N 9/40 Enzymes, e.g. ligases (6.) - acting on alpha-galactose-glycoside bonds, e.g. alpha-galactosidase

A61K 38/47 Medicinal preparations containing peptides

A61K 48/00 Medicinal preparations containing genetic material which is inserted into cells of the living body to treat genetic diseases

C12N 5/10 Undifferentiated human, animal or plant cells, e.g. cell lines - Cells modified by introduction of foreign genetic material, e.g. virus-transformed cells

C12N 15/56 Mutation or genetic engineering - acting on glycosyl compounds (3.2), e.g. amylase, galactosidase, lysozyme

C12N 15/62 Mutation or genetic engineering - DNA sequences coding for fusion proteins